Delivering gene-editing tools to mice while they were still developing in the womb corrected the mutated CFTR gene that causes cystic fibrosis (CF), with the correction lasting into adulthood and restoring normal protein function in the lungs and digestive system, a study found. While it’s still too early…
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Alyftrek has been approved by the European Commission to treat cystic fibrosis (CF) patients 6 years and older who have at least one non-class 1 mutation in the CFTR gene. This indication in the European Union (EU) represents the broadest label for Alyftrek (vanzacaftor/tezacaftor/deutivacaftor) in the world, according to the…
More than a third of caregivers of children with cystic fibrosis (CF) reported delays in getting information about the diagnosis after a positive newborn screening (NBS) test for the disease, according to a study in the U.S. Caregivers mentioned delays in receiving their child’s CF diagnosis and in…
Before my double-lung transplant eight years ago, I notoriously sacrificed my health for my job. I attempted to keep up with the able-bodied people around me, ignoring my limitations, and pushing past what my body could endure. And I paid the price for it. I learned the hard way…
Becoming educated and informed about cystic fibrosis is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your CF journey.
There is no cure for CF yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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